Health & Medicine Six Eyes, One Dose, a Cane Left at the Door Three adults treated with OPGx-LCA5 still showed visual gains at 24 months, Opus Genetics said on 15 October. Six patients in total. Phase 3 has not dosed.
glaucoma Three People, One Injection, and a Safety Board That Said Continue Life Biosciences reported the first human data for ER-100, a partial reprogramming injection, in three people with glaucoma. No serious adverse events at day 56. Two showed visual-field gains. It is not a cure.
gene therapy First Successful Pivotal Gene Therapy for a Blinding Eye Disease Restores Night Vision Beacon's laru-zova helped 31% of high-dose patients gain 15 letters of low-light vision — versus none in the control group.
Health & Medicine / Science & Technology 2026 Breakthrough Prize Winners: Gene Therapies Transform Lives The 2026 Breakthrough Prize honours scientists whose gene therapies have cured blindness and blood disorders, transforming incurable diseases into treatable conditions.
Health & Medicine Gene Therapy Shows Promise for Limb-Girdle Muscular Dystrophy Atamyo's ATA-200 shows clinical benefits with no serious side effects in early trial
Health & Medicine FDA Proposes New Framework to Speed Rare Disease Gene Therapy Approvals "Baby KJ" case demonstrates how personalized CRISPR therapy could become accessible to millions with rare diseases
Health & Medicine Scientists Turn Brain Cells Into Alzheimer's Plaque Cleaners Scientists have developed a groundbreaking approach to treating Alzheimer's disease by converting ordinary brain cells into specialized plaque-clearing machines. This innovative therapy could transform Alzheimer's treatment from a cycle of external interventions to a self-sustaining, internal defense system against the disease's characteristic amyloid plaques.
Health & Medicine Texas Researchers Turn Coffee Into Precision Gene Therapy Controller Everyday caffeine becomes the key to safer, personalized cancer treatment
