The Bright Side

The Bright Side

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FDA Approves AVLAYAH: First Hunter Syndrome Treatment to Cross Blood-Brain Barrier
rare-disease

FDA Approves AVLAYAH: First Hunter Syndrome Treatment to Cross Blood-Brain Barrier

FDA Approves AVLAYAH: First Hunter Syndrome Treatment to Cross Blood-Brain Barrier Revolutionary therapy overcomes 20-year treatment gap for rare genetic disease The US Food and Drug Administration has granted accelerated approval to AVLAYAH™ (tividenofusp-alfa-eknm), marking a watershed moment in rare disease treatment. This is the first FDA-approved biologic specifically designed
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